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Podcast: Foundation Fighting Blindness
Episode: Beacon Therapeutics Reports Encouraging Interim Results from Phase 2 Clinical Trial for XLRP
Description: Beacon Therapeutics has reported vision improvements for five of eight patients receiving the high dose of its X-linked retinitis pigmentosa (XLRP) gene therapy in the Phase 2 SKYLINE clinical trial. Known as AGTC-501, the emerging gene therapy is for patients with mutations in RPGR, the gene most frequently associated with XLRP. Interim, 12-month results for SKYLINE were reported on February 7, 2024, by Mark Pennesi, MD, PhD, director, Ophthalmic Genetics at the Retina Foundation of the Southwest, at the 47th Macula Society Meeting.