Want to create an interactive transcript for this episode?
Podcast: WCG Talks Trials
Episode: Developing Novel Treatments for Rare Disorders: A Look at MPS I with Dr. Emil Kakkis
Description: In this episode, WCGās President of Patient Advocacy, Steve Smith, talks with Emil Kakkis, MD, PhD, Chief Executive Officer of Ultragenyx Pharmaceuticals and President of the non-profit EveryLife Foundation for Rare Diseases organization. Known for his work in developing an enzyme replacement therapy for the rare disorder MPS I and his connection to the Ryan Foundation, Dr. Kakkis shares with us his experiences in being involved in bringing drugs to market and forming relationships with patients along the way.Ā